Stem Cell Therapy for Genetic Disorders
Related Conditions: 유Genetic disorders, Huntington’s disease, cystic fibrosis, amyotrophic lateral sclerosis (ALS), sickle cell anemia, hemophilia, Marfan syndrome, Turner syndrome, Down syndrome, Klinefelter syndrome, Wilson’s disease, phenylketonuria (PKU), Gaucher disease, Tay-Sachs disease, Prader-Willi syndrome, Angelman syndrome, neurofibromatosis, fragile X syndrome, Alport syndrome, Becker muscular dystrophy, Duchenne muscular dystrophy, Rett syndrome, spinal muscular atrophy (SMA).
Efficacy of Stem Cells: Stem cells possess the remarkable ability to differentiate into various cell types, regenerate damaged tissues, and restore lost functions. In the context of genetic disorders, stem cells may help compensate for defective genes by regenerating affected tissues and decelerating disease progression. The goal of stem cell therapy is to repair tissues damaged by genetic mutations and support organ functionality.
Mechanism of Stem Cell Therapy for Genetic Disorders: Stem cells transform into functional cells, replacing those damaged or malfunctioning due to genetic disorders. By introducing healthy cells, stem cell therapy can mitigate the effects of genetic mutations, restoring tissue function and enhancing long-term health.